New York, Jan. 26, 2026 (GLOBE NEWSWIRE) -- In recognition of Rare Disease Day on February 28, the Muscular Dystrophy Association (MDA) is sharing powerful community stories throughout the month that ...
Sarepta reports positive, statistically significant results in a study evaluating the efficacy of its blockbuster gene ...
Jan 26 (Reuters) - Sarepta Therapeutics' gene therapy for a progressive muscle‑wasting disorder showed sustained benefit in ...
"Muscular dystrophy can take many things from me, but it will not take away my happiness, nor will it take away my faith." ...
Genethon highlights latest developments in gene therapies for diseases once considered incurable, including Duchenne muscular dystrophy ...
Disability advocate TaLisha Gryzb is a mother of four living with muscular dystrophy who educates viewers about her ...
In research published in Developmental Medicine & Child Neurology, investigators have developed a brief, reliable, and valid ...
Dr. Michio Hirano to receive the MDA Legacy Award for Achievement in Clinical Research; Allison Moore to receive the MDA ...
Researchers at Kumamoto University have demonstrated that iron supplementation can significantly alleviate muscle pathology and functional decline in a mouse model of facioscapulohumeral muscular ...
The muscular dystrophies are commonly associated with cardiovascular complications, including cardiomyopathy and cardiac arrhythmias. These complications are caused by intrinsic defects in ...
Your muscles need continuous maintenance to stay strong and healthy. Duchenne muscular dystrophy (DMD) happens when there is a change in a person's genetic instructions that affects the production of ...
Zeleciment basivarsen (z-basivarsen) demonstrated sustained functional improvement across multiple clinical measures in the ongoing ACHIEVE ...